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Thesis

Structure-aware and interpretable machine learning for CRISPR-Cas9 cleavage activity prediction

Abstract:

The approval of the ex vivo CRISPR-based gene therapy Casgevy in 2023 shows the potential of CRISPR-based cures for genetic diseases. However, off-target effects induced by heteroduplex mismatches tolerated by Cas9 nucleases limit clinical adoption of the genome editing technology. Despite the advances in developing accurate CRISPR-Cas9 cleavage activity tools and determining factors influencing Cas9 cleavage activity, most tools remain confined to features relating to the spacer-target inter...

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Institution:
University of Oxford
Division:
MPLS
Department:
Computer Science
Oxford college:
Keble College
Role:
Author
ORCID:
0000-0003-0459-9789

Contributors

Institution:
University of Oxford
Division:
MPLS
Department:
Computer Science
Role:
Supervisor
ORCID:
0000-0002-1779-6741


DOI:
Type of award:
DPhil
Level of award:
Doctoral
Awarding institution:
University of Oxford

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