Journal article icon

Journal article

Handling an uncertain control group event risk in non-inferiority trials: non-inferiority frontiers and the power-stabilising transformation

Abstract:

Background

Non-inferiority trials are increasingly used to evaluate new treatments that are expected to have secondary advantages over standard of care, but similar efficacy on the primary outcome. When designing a non-inferiority trial with a binary primary outcome, the choice of effect measure for the non-inferiority margin (e.g. risk ratio or risk difference) has an important effect on sample size calculations; furthermore, if the control event risk observed is m...

Expand abstract
Publication status:
Published
Peer review status:
Peer reviewed

Actions


Access Document


Files:
Publisher copy:
10.1186/s13063-020-4070-4

Authors


More by this author
Institution:
University of Oxford
Division:
MSD
Department:
NDM
Sub department:
NDM Experimental Medicine
Role:
Author
ORCID:
0000-0002-0412-8509


Publisher:
BioMed Central
Journal:
Trials More from this journal
Volume:
21
Article number:
145
Publication date:
2020-02-06
Acceptance date:
2020-01-13
DOI:
EISSN:
1745-6215


Language:
English
Keywords:
Pubs id:
pubs:1082191
UUID:
uuid:9a5b059c-02b4-47e2-a977-45e3998f2996
Local pid:
pubs:1082191
Source identifiers:
1082191
Deposit date:
2020-01-13

Terms of use



Views and Downloads






If you are the owner of this record, you can report an update to it here: Report update to this record

TO TOP