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Journal article

Therapeutic approaches to muscular dystrophy.

Abstract:

Muscular dystrophies are a heterogeneous group of genetic disorders characterized by muscle weakness and wasting. Duchenne muscular dystrophy (DMD) is the most common and severe form of muscular dystrophy, and although the molecular mechanisms of the disease have been extensively investigated since the discovery of the gene in 1986, there is currently no effective treatment. However, new gene-based therapies have recently emerged with particular noted advances in using conventional gene repla...

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Publication status:
Published

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Publisher copy:
10.1093/hmg/ddr105

Authors


More by this author
Institution:
University of Oxford
Division:
MSD
Department:
Physiology Anatomy & Genetics
Role:
Author
Journal:
Human molecular genetics More from this journal
Volume:
20
Issue:
R1
Pages:
R69-R78
Publication date:
2011-04-01
DOI:
EISSN:
1460-2083
ISSN:
0964-6906
Language:
English
Keywords:
Pubs id:
pubs:127193
UUID:
uuid:0b20898a-8651-437b-ad4c-67b0752fdad0
Local pid:
pubs:127193
Source identifiers:
127193
Deposit date:
2012-12-19

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