An LNA-amide modification that enhances the cell uptake and activity of phosphorothioate exon-skipping oligonucleotides (Nature Communications, 2022)

(untitled) - Baker, YR; Thorpe, C; Chen, J; Poller, LM; Cox, L; Kumar, P; Lim, WF; Lie, L; McClorey, G; Epple, S; Singleton, D; McDonough, MA; et al.