Journal article icon

Journal article

An organelle-specific protein landscape identifies novel diseases and molecular mechanisms

Abstract:
Cellular organelles provide opportunities to relate biological mechanisms to disease. Here we use affinity proteomics, genetics and cell biology to interrogate cilia: poorly understood organelles, where defects cause genetic diseases. Two hundred and seventeen tagged human ciliary proteins create a final landscape of 1,319 proteins, 4,905 interactions and 52 complexes. Reverse tagging, repetition of purifications and statistical analyses, produce a high-resolution network that reveals organelle-specific interactions and complexes not apparent in larger studies, and links vesicle transport, the cytoskeleton, signalling and ubiquitination to ciliary signalling and proteostasis. We observe sub-complexes in exocyst and intraflagellar transport complexes, which we validate biochemically, and by probing structurally predicted, disruptive, genetic variants from ciliary disease patients. The landscape suggests other genetic diseases could be ciliary including 3M syndrome. We show that 3M genes are involved in ciliogenesis, and that patient fibroblasts lack cilia. Overall, this organelle-specific targeting strategy sh ows considerable promise for Systems Medicine.
Publication status:
Published
Peer review status:
Peer reviewed

Actions


Access Document


Publisher copy:
10.1038/ncomms11491

Authors


More by this author
Role:
Author
ORCID:
0000-0002-0658-4399



Publisher:
Nature Publishing Group
Journal:
Nature Communications More from this journal
Volume:
7
Pages:
11491
Publication date:
2016-05-13
Acceptance date:
2016-04-01
DOI:
ISSN:
2041-1723


Keywords:
Pubs id:
pubs:844994
UUID:
uuid:caec74e1-9769-4049-8f27-7acb51d09a31
Local pid:
pubs:844994
Source identifiers:
844994
Deposit date:
2018-05-14

Terms of use



Views and Downloads






If you are the owner of this record, you can report an update to it here: Report update to this record

TO TOP