Correction of amyotrophic lateral sclerosis related phenotypes in induced pluripotent stem cell-derived motor neurons carrying a hexanucleotide expansion mutation in C9orf72 by CRISPR/Cas9 genome editing using homology-directed repair (Human Molecular Genetics, 2020)

(untitled) - Ababneh, NA; Scaber, J; Flynn, R; Douglas, A; Barbagallo, P; Candalija, A; Turner, MR; Sims, D; Dafinca, R; Cowley, SA; Talbot, KA