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A randomised, double-blind, placebo-controlled phase IIB clinical trial of repeated application of gene therapy in patients with cystic fibrosis

Abstract:
The UK Cystic Fibrosis Gene Therapy Consortium has been working towards clinical gene therapy for patients with cystic fibrosis for several years. We have recently embarked on a large, multi-dose clinical trial of a nonviral, liposome-based formulation powered for the first time to detect clinical benefit. The article describes the details of the protocol.

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Authors


Alton, EWFW More by this author
Cunningham, S More by this author
Davies, JC More by this author
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Journal:
Thorax
Volume:
68
Issue:
11
Pages:
1075-1077
Publication date:
2013-11-05
DOI:
EISSN:
1468-3296
ISSN:
0040-6376
URN:
uuid:803f1c60-7b1e-4a3b-8834-eb1d0b289182
Source identifiers:
436297
Local pid:
pubs:436297
Language:
English

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