An analysis of retinal gene therapy clinical trials.
In 2008, the initial results from the first three gene therapy trials to use adeno-associated viral vectors to treat an inherited retinal degeneration were published. These trials demonstrated no significant vector-related side effects and provided evidence of successful gene transfer with improved vision in several patients. The success of these trials heralds the beginning of a new era in the treatment of retinal diseases. Much can be learnt by comparing the results of the individual studie...Expand abstract
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- Current opinion in molecular therapeutics
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