Ataluren, a new therapeutic for alpha-1 antitrypsin deficient individuals with nonsense mutations (American Journal of Respiratory and Critical Care Medicine, 2018)

(untitled) - Reeves, E; O’Dwyer, C; Dunlea, D; Wormald, M; Hawkins, P; Alfares, M; Kotton, D; Rowe, S; Wilson, A; McElvaney, N