Nusinersen in patients older than 7 months with spinal muscular atrophy type 1: A cohort study (Neurology, 2018)

(untitled) - Aragon-Gawinska, K; Seferian, AM; Daron, A; Gargaun, E; Vuillerot, C; Cances, C; Ropars, J; Chouchane, M; Cuppen, I; Hughes, I; Illingworth, M; Marini-Bettolo, C; et al.