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Next‐generation sequencing for the diagnosis of MYH9‐RD: Predicting pathogenic variants

Abstract:

The heterogeneous manifestations of MYH9‐related disorder (MYH9‐RD), characterized by macrothrombocytopenia, Döhle‐like inclusion bodies in leukocytes, bleeding of variable severity with, in some cases, ear, eye, kidney, and liver involvement, make the diagnosis for these patients still challenging in clinical practice. We collected phenotypic data and analyzed the genetic variants in more than 3,000 patients with a bleeding or platelet disorder. Patients were enrolled in the BRIDGE‐BPD and T...

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Publication status:
Published
Peer review status:
Peer reviewed

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Publisher copy:
10.1002/humu.23927

Authors


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Role:
Author
ORCID:
0000-0003-0333-0948
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Role:
Author
ORCID:
0000-0002-2826-3879
Publisher:
Wiley
Journal:
Human Mutation More from this journal
Volume:
41
Issue:
1
Pages:
277-290
Publication date:
2019-10-15
Acceptance date:
2019-09-25
DOI:
EISSN:
1098-1004
ISSN:
1059-7794
Pmid:
31562665
Language:
English
Keywords:
Pubs id:
1090489
Local pid:
pubs:1090489
Deposit date:
2020-03-06

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